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ATMP Seminar - Coggle Diagram
ATMP Seminar
ATMPs
Gene therapy medicinal products - most succesful
Tx inherited disease
Cancer therapies
Tissue regeneration
Somatic cell therapy medicinal producs
Cartilage defects
Immune disease
Tx parkinsons / azd
Cardiac repair
Skin replacement
Cancer imunotherapy - haematological
Tissue engineered products - least successful
Gene Therapy Medicinal Products
Glybera
Use
tx of lipoprotein lipase deficiency
In vivo gene therapies
Too costly - taken off market
Strimvelis
Use
ADA-SCID
Ex vivo gene therapy
Small Molecule Drugs / Small Oligonucleotides
Examples
Hyperlipidaemia
Duchenne - exon skippers